Improved Criteria for the Classification of Titin Variants in Inherited Skeletal Myopathies

Marco Savarese, Mridul Johari, Katherine Johnson, Meharji Arumilli, Annalaura Torella, Ana Töpf, Anna Rubegni, Marius Kuhn, Teresa Giugliano, Dieter Gläser, Fabiana Fattori, Rachel Thompson, Sini Penttilä, Sara Lehtinen, Sara Gibertini, Alessandra Ruggieri, Marina Mora, Ales Maver, Borut Peterlin, Ami MankodiHanns Lochmüller, Filippo Maria Santorelli, Benedikt Schoser, Lenka Fajkusová, Volker Straub, Vincenzo Nigro, Peter Hackman, Bjarne Udd

Research output: Contribution to journalArticleScientificpeer-review

Original languageEnglish
JournalJournal of Neuromuscular Diseases
Volume7
Issue number2
Pages (from-to)153-166
Number of pages14
ISSN2214-3599
DOIs
Publication statusPublished - 2020
MoE publication typeA1 Journal article-refereed

Fields of Science

  • cardiomyopathies
  • clinical interpretation
  • data sharing
  • skeletal muscle disorders
  • Titin
  • connectin
  • TTN protein, human
  • adult
  • Article
  • case control study
  • cohort analysis
  • conceptual framework
  • controlled study
  • disease classification
  • gene frequency
  • genetic analysis
  • genetic association
  • genetic disorder
  • genetic heterogeneity
  • genetic variability
  • human
  • major clinical study
  • medical school
  • medical society
  • molecular pathology
  • myopathy
  • population based case control study
  • population genetics
  • practice guideline
  • priority journal
  • quantitative analysis
  • standardization
  • TTN gene
  • cardiomyopathy
  • classification
  • genetics
  • muscle disease
  • Cardiomyopathies
  • Connectin
  • Humans
  • Muscular Diseases
  • Practice Guidelines as Topic
  • 1182 Biochemistry, cell and molecular biology

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