The Phenotype of Dysferlin-Deficient Mice Is Not Rescued by Adeno-Associated Virus-Mediated Transfer of Anoctamin 5

Francois Monjaret, Laurence Suel-Petat, Nathalie Bourg-Alibert, Anna Vihola, Sylvie Marchand, Carinne Roudaut, Evelyne Gicquel, Bjarne Udd, Isabelle Richard, Karine Charton

Research output: Contribution to journalArticleScientificpeer-review

Original languageEnglish
JournalHuman gene therapy. Clinical development
Volume24
Issue number2
Pages (from-to)65-76
Number of pages12
ISSN2324-8637
DOIs
Publication statusPublished - Jun 2013
MoE publication typeA1 Journal article-refereed

Fields of Science

  • GIRDLE MUSCULAR-DYSTROPHY
  • SKELETAL-MUSCLE
  • MIYOSHI MYOPATHY
  • MEMBRANE REPAIR
  • GNATHODIAPHYSEAL-DYSPLASIA
  • GENE-TRANSFER
  • C2 DOMAINS
  • T-TUBULE
  • PROTEIN
  • FAMILY
  • 3111 Biomedicine

Cite this